TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease
Por um escritor misterioso
Descrição
Children with Niemann-Pick Type C (NPC), their parents and scientists seeking a treatment for this fatal genetic disease. WSJ follows this 6-year fight.
Niemann-Pick disease type C, Orphanet Journal of Rare Diseases
Two-Year-Old Kamryn Living with Niemann-Pick Disease Type C (NPC) - The Children's Inn at NIH
Efficacy and safety of arimoclomol in Niemann‐Pick disease type C: Results from a double‐blind, randomised, placebo‐controlled, multinational phase 2/3 trial of a novel treatment - Mengel - 2021 - Journal of Inherited
PDF) Recent Advances in the Diagnosis and Treatment of Niemann-Pick Disease Type C in Children: A Guide to Early Diagnosis for the General Pediatrician
Rare Disease Video - Niemann-Pick Disease Types A & B - National Organization for Rare Disorders
Niemann–Pick disease - Wikipedia
Genes, Free Full-Text
Your Impact - Ara Parseghian Medical Research Fund
For a Rare Disease, Drug Trials Scramble for Patients - WSJ
de
por adulto (o preço varia de acordo com o tamanho do grupo)
