Niemann-Pick disease type C. The diagram represents subtypes and
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Niemann-Pick disease type C as a neurovisceral disease. Schematic
Cancers, Free Full-Text
Cellular Adaptations and Accumulations Flashcards
Niemann-Pick Disease, Types A and B
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Skeletal manifestations in pediatric and adult patients with Niemann Pick disease type B - Wasserstein - 2013 - Journal of Inherited Metabolic Disease - Wiley Online Library
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Frontiers Neuronopathic Gaucher disease: Beyond lysosomal dysfunction
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